2 New Gene Therapies to Treat Sickle Cell Disease


The gene-based treatments include medications Lyfgenia, the first that uses the gene-editing technique CRISPR, and Casgevy.

An estimated 1 of every 365 Black babies born in the US have sickle cell. Patients aged 12 and older with histories of vaso-occlusive crises potentially qualify for this new treatment.

Medical researchers will follow patients who receive Casgevy or Lyfgenia in a long-term study to evaluate each product’s safety and effectiveness. More information is here.


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